Jan 17 (Reuters) - PHARNEXT SA PHARN.PA :
* NEW DATA PUBLISHED IN PLOS ONE DEMONSTRATES EARLY
THERAPEUTIC
EFFECTS OF PHARNEXT'S PLEODRUG(TM) PXT3003 IN A TRANSGENIC RAT
MODEL OF CHARCOT-MARIE-TOOTH DISEASE TYPE 1A
* LOOKS FORWARD TO INITIATING A PHASE 3 TRIAL OF PXT3003 IN
PEDIATRIC PATIENTS BY END OF 2019
* INTENDS TO LAUCH A PEDIATRIC PHASE 3 CLINICAL TRIAL IN
CHILDREN
TO INVESTIGATE SAFETY AND EFFICACY OF PXT3003
* NEW PRECLINICAL RESULTS FOR ITS LEAD PLEODRUG(TM) PXT3003
IN
PLOS ONE SHOWING THAT EARLY TREATMENT WITH PXT3003 IN TRANSGENIC
RAT MODEL DELAYS ONSET OF CMT1A
* INVESTIGATION PLAN WAS AGREED WITH EUROPEAN MEDICINES
AGENCY
Source text for Eikon: ID:nEQVY2lya
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