Brief: Poxel's PXL065, PXL770 Granted Orphan Drug Designation By FDA
May 17 (Reuters) - Poxel SA POXEL.PA :
* ANNOUNCES PXL065 AND PXL770 GRANTED ORPHAN DRUG
DESIGNATION FROM
THE U.S. FDA FOR X-LINKED ADRENOLEUKODYSTROPHY
* BOTH COMPOUNDS ARE PREPARING TO ENTER INTO PHASE 2A
CLINICAL
PROOF-OF-CONCEPT (POC) BIOMARKER STUDIES AS SOON AS POSSIBLE,
SUBJECT TO FINANCING
Source text for Eikon: ID:nBw5fKBBha
Further company coverage: POXEL.PA
(Gdansk Newsroom)
((gdansk.newsroom@thomsonreuters.com; +48587696600;))
Recent news on Poxel SA
See all newsFrance's Poxel Q3 revenue rises on higher TWYMEEG royalties
France's Poxel Q2 revenue rises on higher TWYMEEG royalties
France's Poxel Q1 revenue rises 20% on TWYMEEG sales
Brief: Poxel Announces That A Combined General Meeting Will Be Held On December 11, 2025 And The Availability Of The Preparatory Documents
Brief: Poxel Says Cash Runway Estimated Between Mid To End Q2 2025