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DSGN — Design Therapeutics News Story

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Brief: Design Therapeutics Reports Positive Data From Single-Ascending Dose Trial Of DT-216 For The Treatment Of Friedreich Ataxia And Portfolio Progress

Dec 7 (Reuters) - Design Therapeutics Inc  DSGN.O :
    * DESIGN THERAPEUTICS REPORTS POSITIVE DATA FROM
SINGLE-ASCENDING
DOSE TRIAL OF DT-216 FOR THE TREATMENT OF FRIEDREICH ATAXIA AND
PORTFOLIO PROGRESS
    * DESIGN THERAPEUTICS INC - ADVANCING MYOTONIC DYSTROPHY
TYPE-1
GENETAC(TM) LEAD MOLECULES; IND EXPECTED IN 2024
    * DESIGN THERAPEUTICS INC - DT-216 WAS GENERALLY
WELL-TOLERATED
AND RESULTED IN A MORE THAN DOUBLING OF FRATAXIN MRNA IN
PATIENTS WITH FRIEDREICH ATAXIA
    * DESIGN THERAPEUTICS-DT-168, FOR TREATMENT OF FUCHS
ENDOTHELIAL
CORNEAL DYSTROPHY ADMINISTERED AS AN EYE DROP DROP IN TRIAL;
EXPECTS IND IN 2023

Source text for Eikon:  ID:nGNXgzxVt 
Further company coverage:  DSGN.O 
 ((Reuters.Briefs@thomsonreuters.com;;))

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