** Shares of gene therapy company MeiraGTx Holdings plc
MGTX.O up 13.6% at $7.76 premarket
** Co says
early-stage study
data for its experimental gene therapy, rAAV8.hRKp.AIPL1,
showed safety, efficacy and meaningful responses for treatment
of genetic eye condition called retinal dystrophy
** Says children who were blind at birth were treated
with the gene therapy and showed visual acuity in eyes after
four or more weeks in small study
** The therapy showed improved functional vision and
evidence of protection against progressive retinal degeneration,
without serious adverse effects
** Retinal dystrophy is caused due to genetic deficiency of
type of protein called AIPL1, which leads severe impairment of
sight from birth
** Co says study data is published in medical journal The
Lancet
** MGTX stock has risen ~16% in last 12 months
(Reporting by Siddhi Mahatole)
((Siddhiprabhanjan.mahatole@thomsonreuters.com))