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NVS — Novartis AG News Story

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Brief: Novartis Provides Update On Delpacibart Etedesiran (Del-Desiran) Phase Iii Harbor Study

BRIEF-Novartis Provides Update On Delpacibart Etedesiran (Del-Desiran) Phase Iii Harbor Study

- NOVARTIS AG NOVN.S:

  • PROVIDES UPDATE ON DELPACIBART ETEDESIRAN (DEL-DESIRAN) PHASE III HARBOR STUDY FOR THE TREATMENT OF MYOTONIC DYSTROPHY TYPE 1 (DM1)

  • HARBOR PHASE III STUDY DID NOT MEET PRIMARY ENDPOINT IN DM1

  • DEL-DESIRAN SHOWED EVIDENCE OF CLINICAL ACTIVITY IN SECONDARY ENDPOINTS

  • MAINTAINS 5-6% FIVE-YEAR SALES CAGR GUIDANCE FOR 2025-2030

  • FDA GRANTS PRIORITY REVIEW FOR DELPACIBART ZOTADIRSEN IN DMD44

Source text: ID:nGNE9BzK3V

Further company coverage: NOVN.S


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