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RCKT — Rocket Pharmaceuticals News Story

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Brief: Rocket Pharmaceuticals Announces Positive Clinical Safety Update From Initial Three Patients Treated With Rp-A501 Under Modified Phase 2 Protocol For Danon Disease

BRIEF-Rocket Pharmaceuticals Announces Positive Clinical Safety Update From Initial Three Patients Treated With Rp-A501 Under Modified Phase 2 Protocol For Danon Disease

- Rocket Pharmaceuticals Inc RCKT.O:

  • ROCKET PHARMACEUTICALS ANNOUNCES POSITIVE CLINICAL SAFETY UPDATE FROM INITIAL THREE PATIENTS TREATED WITH RP-A501 UNDER MODIFIED PHASE 2 PROTOCOL FOR DANON DISEASE

  • ROCKET PHARMACEUTICALS - RP-A501 WELL-TOLERATED IN INITIAL THREE PATIENTS WITH NO TMA OR CAPILLARY LEAK SYNDROME

  • ROCKET PHARMACEUTICALS - ENGAGING WITH FDA ON PIVOTAL TRIAL; REGULATORY UPDATE EXPECTED IN H2 2026

  • ROCKET PHARMACEUTICALS - DANON DISEASE PROGRAM UPDATE EXPECTED IN H2 2026

Source text: ID:nBw9cyXvYa

Further company coverage: RCKT.O


((Reuters.Briefs@thomsonreuters.com;))

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