Brief: Sio Gene Therapies Announces Positive Interim Safety And Biomarker Data From Ongoing Phase 1/2 Clinical Study Of AXO-AAV-GM1 Gene Therapy In GM1 Gangliosidosis
Oct 21 (Reuters) - Sio Gene Therapies Inc SIOX.O :
* SIO GENE THERAPIES ANNOUNCES POSITIVE INTERIM SAFETY AND
BIOMARKER DATA FROM ONGOING PHASE 1/2 CLINICAL STUDY OF
AXO-AAV-GM1 GENE THERAPY IN GM1 GANGLIOSIDOSIS
* SIO GENE THERAPIES - AXO-AAV-GM1 GENERALLY WELL-TOLERATED
AT
BOTH LOW AND HIGH DOSES WITH MAJORITY OF ADVERSE EVENTS
CONSIDERED MILD TO MODERATE
* NO ADVERSE EVENTS LEADING TO STUDY WITHDRAWAL IN ANY
PATIENTS
* BASED ON RESULTS OF THE STUDY WORKING ON CONTINUED
DEVELOPMENT
OF AXO-AAV-GM1 AND PLAN TO ENGAGE FDA
Source text for Eikon: ID:nGNX8MBzDD
Further company coverage: SIOX.O
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