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RARE — Ultragenyx Pharmaceutical News Story

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Brief: Ultragenyx Announces Phase 3 Aspire Results In Angelman Syndrome

BRIEF-Ultragenyx Announces Phase 3 Aspire Results In Angelman Syndrome

- Ultragenyx Pharmaceutical Inc. RARE.O:

  • ULTRAGENYX ANNOUNCES PHASE 3 ASPIRE RESULTS IN ANGELMAN SYNDROME

  • ULTRAGENYX PHARMACEUTICAL - PHASE 3 ASPIRE STUDY DID NOT ACHIEVE PRIMARY OR KEY SECONDARY ENDPOINTS

  • ULTRAGENYX PHARMACEUTICAL - SAFETY PROFILE IN ASPIRE STUDY CONSISTENT WITH PHASE 1/2

  • ULTRAGENYX PHARMACEUTICAL - TO EVALUATE APAZUNERSEN PROGRAM AND IMPLEMENT SIGNIFICANT EXPENSE REDUCTIONS

  • ULTRAGENYX PHARMACEUTICAL - EXPECTS TO CONTINUE TOWARD PROFITABILITY IN 2027

Source text: ID:nGNX5gyGjV

Further company coverage: RARE.O


((Reuters.Briefs@thomsonreuters.com;))

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