US FDA declines to approve Ultragenyx's gene therapy for rare genetic disorder
11/07/2025 21:37
July 11 (Reuters) - The U.S. Food and Drug Administration has declined to approve Ultragenyx Pharmaceutical's RARE.O experimental gene therapy to treat a rare genetic disorder, the company said on Friday. (Reporting by Kamal Choudhury in Bengaluru; Editing by Shailesh Kuber) ((Kamal.Choudhury@thomsonreuters.com;))
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