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PHARM — Pharming News Story

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Brief: Pharming Presents Positive Phase II Topline Data For Leniolisib

BRIEF-Pharming Presents Positive Phase II Topline Data For Leniolisib

- Pharming Group N.V. PHAR.AS:

  • PRESENTS POSITIVE PHASE II TOPLINE DATA FOR LENIOLISIB IN GENETIC PIDS WITH IMMUNE DYSREGULATION AT ESID 2026

  • LENIOLISIB WELL-TOLERATED WITH BENEFITS IN IMMUNE DYSREGULATION MEASURES

  • MEAN SPLEEN VOLUME REDUCTION OF 26.4% IN PHASE II LENIOLISIB TRIAL

  • IMPROVEMENT IN LIVER STIFFNESS OBSERVED IN PHASE II LENIOLISIB TRIAL

  • MEAN LYMPH NODE LESION SIZE REDUCTION OF 33.7% IN PHASE II LENIOLISIB TRIAL

  • MEAN DLCO INCREASED BY 8.0% IN PHASE II LENIOLISIB TRIAL

  • ALL PHASE II LENIOLISIB STUDY COMPLETERS ENROLLED IN THREE-YEAR EXTENSION STUDY

  • LENIOLISIB WAS GENERALLY WELL-TOLERATED ACROSS ALL 4 GENOTYPES

  • TOPLINE RESULTS FROM SEPARATE PHASE II TRIAL IN CVID EXPECTED IN NOVEMBER

Source text: ID:nGNE6y1QPF

Further company coverage: PHAR.AS


(Gdansk Newsroom)

((gdansk.newsroom@thomsonreuters.com; +48 58 769 66 00;))

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